X4 Pharmaceuticals’ Post

Exciting week to talk about #scleroderma and rare musculoskeletal diseases. Hopefully see many of you in Prague! #clinicaltrials #imaging #cartcelltherapy #innovation #pharma #biotechnology

Check out the recording of our session with Kate Shaw, Founder and CEO of Innovative Trials and Leanne Woehlke, Director of Life Science Solutions at TPT. This webinar examines current challenges to meeting and retaining recruitment numbers, and how clinical sites can strive to ensure patients are kept at the core of their operations. https://lnkd.in/ezaiA6A5 #patientengagement #clinicaltrials #webinar

Consilium Scientific in conversation with Frank Harrell: Modernizing Clinical Trial Design and Analysis to Improve Efficiency & Flexibility. This talk covers several ways to make clinical trials more efficient and to reduce the chance of ending with an equivocal result. Some of the approaches covered are Bayesian sequential designs allowing for study extension if results are promising, not being tied by type I assertion probabilities/α spending, using high-information longitudinal ordinal outcomes, and covariate adjustment.

Don't miss the FINAL part of our three-part series "Thriving in Clinical Research - Overcoming Common Challenges as a Site." This final session addresses a top site challenge identified in our 2023 Site Challenges Survey: Site Capacity. Hear from industry experts to learn about core considerations for trial success and discover proven solutions to increase trial efficiency and drive transformative results for participants. Join us December 5th, register now at https://lnkd.in/g_49pQpi #ClinicalResearch #SiteChallenges #SiteResourcing

THE RIGHT ANSWER: DEDICATED RESEARCH SITE I fully agree with Torsten Sernau, that today's dedicate d Reseacr site sa is the right response to the changes being made in the field of clinical research. I started my research in 1994. I was the site of one doctor, one nurse, one assistant. This was enough to carry out three protocols three protocols in ibandronate clinicnal trial. At that time, the CRF was 25 pages long and the central documentation was fed into a single CRO computer from carbon copy extracted from the CRF of the local centers. Currently, CRF takes several hundred or even more pages and often does not fit in one binder.  Hence, in 2020, there were 12 doctors and 4 nurses working in my center and 4 coordinators, plus others. Projects are becoming more and more complex and their implementation consumes a huge amount of working time. The only answer to the situation is a Dedicated Research Site.

Results presented at the ESC HFA 2024 late breaker clinical trial session on May 11th! A consistent effect of PA guided therapy across predefined subgroups within and across clinical endpoint categories of QoL, HFH and mean PAP in the MONITOR-HF trial. Please find the draft manuscript simultaneously published in European Heart Journal! https://lnkd.in/eXVk66g5

Read about the latest developments in the NVG-291 clinical study and how you may qualify to be a participant. There's also info in this article on how to listen to the interview on Curecast with Dr. Monica Perez, a clinician-scientist at the Shirley Ryan AbilityLab in Chicago, who discusses this exciting trial in more detail. Check it out HERE - https://bit.ly/48jace5

👉2️⃣0️⃣1️⃣5️⃣, International Atherosclerosis Society (IAS) meeting in #amsterdan 😯My first poster about Lp(a) 5️⃣ patients with very high levels of Lp(a) and different clinical manifestations 💪It is fantastic to see today, 8️⃣years later, many presentations and how science has advanced

https://lnkd.in/e-h3sXjZ In honor of #labweek2024 - a reminder about how vitally important our lab professionals are to innovating the future of so many industries - in this case #diagnosticmedicine. Their efforts to provide critical answers every day should always be celebrated! "Since the pandemic, the awareness of the importance of the lab has grown significantly. Here are just a few of the impacts: -70% of today’s medical decisions depend on laboratory test results. -260,000 CLIA-certified laboratories across the U.S. represent the cornerstone of diagnostic medicine today. -14 billion laboratory tests are ordered annually — safety, quality, and cost-effectiveness in laboratory testing are required for effective diagnosis and treatment of disease." Future Labs Live USA #FutureLabsLive #LabWeek #labinnovation #labtesting #labsafety #labquality #healthandmedicine